Medicine

Accelerating ASO treatments from advancement to execution

.Completing passions.R.S., M.S., H.G. as well as A.A.R. are actually planners of the 1M1M effort. H.G. and also A.A.R. are board of supervisors members and also R.S., M.S. and also A.A.R. are actually participants of the clinical advisory committee of N1C. A.A.R. discloses job through LUMC, which has patents on exon-skipping modern technology, a few of which has actually been actually certified to BioMarin and also consequently sublicensed to Sarepta. As co-inventor of several of these licenses, A.A.R. was actually qualified to an allotment of aristocracies. A.A.R. further reveals serving as consultant for PTC Therapies, Sarepta Therapies, Regenxbio, Dyne Rehabs, Lilly, BioMarin Pharmaceuticals Inc., Eisai, Entrada, Takeda, Splicesense, Galapagos, Sapreme, Italfarmaco and also Astra Zeneca. In the past 5 years, A.A.R. also conducted speaking with for Alpha Anomeric. A.A.R. also reports registration of the clinical boards of advisers of Eisai, Hybridize Therapeutics, Muteness Therapeutics, Sarepta Therapeutics, Sapreme and also Mitorx. In the past 5 years, A.A.R. was also a clinical board of advisers participant for ProQR. Commission for A.A.R. u00e2 s consulting and advising tasks is paid out to LUMC. Over the last 5 years, LUMC additionally got sound speaker honoraria coming from PTC Rehabs, Alnylam Netherlands, Italfarmaco and Pfizer as well as financing for deal study from Sapreme, Eisai, Galapagos, Synaffix and Alpha Anomeric. Venture funding is actually received coming from Sarepta Rehabs and also Entrada via unlimited gives. H.G. has nothing to divulge in regard to the topics dealt with within this document. Over the last 5 years, he has also gotten working as a consultant gratuity coming from UCB. M.S. received consultancy gratuity from Ionis, UCB, Prevail, Orphazyme, Biogen, Servier, Reata, GenOrph, AviadoBio, Biohaven, Zevra, Lilly and Solaxa in the past 5 years, all unassociated to the present manuscript. R.S. possesses nothing to reveal relative to the subject matters covered within this composition. She has received sound speaker and/or working as a consultant gratuity or even financing payments from Abbvie, Bial, STADA and Everpharma previously 5 years.